Researchers have discovered how part of the body's immune system could better combat a leading cause of death for people with ...

A nanobody that stabilizes mutant CFTR from inside the cell, especially when combined with existing drugs, restores near-normal function in cystic fibrosis cells.

Researchers have mapped how lung damage begins early in life for children with cystic fibrosis, providing new insights that will help reshape future care. The research team, led by Murdoch Children's ...

The development of gene editing tools, which enable the specific targeting and correction of mutations, hold the promise of allowing us to correct those mutations that cause genetic diseases. However, ...

Please provide your email address to receive an email when new articles are posted on . Over a 16-year period, those with cystic fibrosis vs. sickle cell disease had a larger improvement in mean age ...

A national study showed decreasing mortality for cystic fibrosis but increasing mortality for sickle cell disease from 2008 to 2023. The trends affected nearly all age groups. The researchers ...

BOSTON--(BUSINESS WIRE)--Porosome Therapeutics, Inc. (Porosome Therapeutics) today announced the publishing of a study that brings promise for a cure to cystic fibrosis (CF). The preprint highlights ...

When UNSW Associate Professor Shafagh Waters explains cystic fibrosis (CF) to the children she works with, she asks them to imagine what is happening inside their own bodies. "I tell them to picture ...

A fundamental challenge for cystic fibrosis (CF) gene therapy is ensuring sufficient transduction of airway epithelial cells to achieve therapeutic correction. Gene editing is a method to permanently ...

While cystic fibrosis has long been Vertex Pharmaceuticals’ bread and butter, the company has been eager to diversify its revenue base in recent years. As several patients start their treatment ...

Australian researchers have mapped how lung damage may begin early in life for children with cystic fibrosis, providing new insights that may help reshape future care.

Researchers have mapped how lung damage begins early in life for children with cystic fibrosis, providing new insights that will help reshape future care.